1
Tirtha Chakraborty, Antonin de Fougerolles, Ron Weiss: Modified polynucleotides for treating galactosylceramidase protein deficiency. Moderna Therapeutics, DT Ward PC, Donna T Ward, Jennifer F Bryan, July 28, 2015: US09089604 (8 worldwide citation)

The invention relates to compositions and methods for the preparation, manufacture and therapeutic use of polynucleotides, primary transcripts and mmRNA molecules.


2
MODIFIED POLYNUCLEOTIDES FOR TREATING GALACTOSYLCERAMIDASE PROTEIN DEFICIENCY. Moderna Therapeutics, August 7, 2014: US20140221465-A1

The invention relates to compositions and methods for the preparation, manufacture and therapeutic use of polynucleotides, primary transcripts and mmRNA molecules.